Rare & Orphan Disease

PharPoint Research > Therapeutic Areas > Rare and Orphan Disease

Providing you with an experienced rare disease team

Rare and orphan disease clinical research presents sponsors with unique challenges due to wide geographical spreads and small, heterogeneous patient populations.

Partnering with a team that lacks the right rare and orphan disease experience may increase a study’s cost due to timeline delays from logistic, strategic, and operational challenges.

The team you meet is the team you get

When working with “big box” CROs, sponsors may find themselves victims of “bait-and-switch” staffing techniques.

Sponsors initially meet with rare disease experts under the assumption those niche industry leaders will be actively involved in study operations. In reality, these experts are often used primarily as marketing tools, while your actual study team is swapped out with junior staff that may not hold any study-specific experience. This approach doesn’t just lack transparency: without the on-hand therapeutic expertise you had anticipated, your risk of lengthy study timelines and higher costs increases.

At PharPoint, we’re honest about the experienced team that will be handling the day-to-day operations of your study. Our clinical team is fully invested in your success—not just the bottom line—and we rely on therapeutically aligned teams who understand how to mitigate the unique challenges rare disease studies bring. Our proactive risk mitigation strategy and well-trained, responsive team helps PharPoint consistently deliver better results.

Meet our talented management team

Access our rare disease experience infographic:
What makes working with PharPoint Research as your rare CRO different?

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